Spinal muscular atrophy (SMA) is a genetic disease that affects the spinal cord and nerves, resulting in muscle wasting and weakness. Untreated, it is a neurodegenerative, progressive disease, which can be fatal in its more severe forms. Children with the most common forms, type 1 and type 2 SMA, either never achieve sitting or can sit ... Cure SMA is excited to announce that we will reunite the SMA community in-person for the 2022 Annual SMA Conference in Anaheim, CA–Thursday, June 16 through Sunday, June 19, 2022. If the unexpected circumstances surrounding the pandemic have shown us anything, it is how impactful this one week of the…The Cure SMA Walk-n-Roll is a fun, family-friendly event that supports Cure SMA’s mission of driving breakthroughs in treatment and care and providing families the support they need for today. We welcome you to join us as an individual or start a team with your family, friends, co-workers, and neighbors.The…SMA is a rare genetic disease caused by a mutation in the survival motor neuron 1 (SMN1) gene. The gene encodes the survival motor neuron (SMN) protein – a protein found throughout the body ...We are pleased to share the following SMA community letter from our partners at Genentech on their clinical development programs and initiatives. Dear SMA Community, Summer is upon us and so are a number of developments we are pleased to share with the SMA community. We are enjoying interacting with…New Zolgensma data demonstrate age-appropriate development when used early, real-world benefit in older children, and durability 5+ years post-treatment. Novartis Gene Therapies recently shared new data that reinforce the transformational benefit of Zolgensma (onasemnogene abeparvovec), a one-time treatment for spinal muscular …Cure SMA and its partners in industry, healthcare, and research created the Clinical Trial Readiness Program to increase the number of well-prepared, patient-centered SMA clinical trial sites. Increasing the number of clinical trial sites will make SMA research participation an option for more SMA-affected individuals, accelerating the progress ...Cure SMA and our partners in the SMA Industry Collaboration are pleased to announce the release of the Spinal Muscular Atrophy Voice of the Patient (VoP) Report. This report is a thorough written account of the Patient-Focused Drug Development (PFDD) Meeting with the FDA, in the spring of 2017. Patient…The presentation will draw from the community viewpoints we have collected from focus groups, surveys, and the Voices of SMA project. Cure SMA also provided funding support for this meeting. The workshop will take place at EMA’s premises in London on November 11, 2016. The entire day will be broadcast live and can be seen on the EMA’s website.Cure SMA is a nonprofit organization that provides information, support, and research for spinal muscular atrophy (SMA), a genetic condition that affects the motor nerve …SMA type 2 is a less common form of SMA. Symptoms begin later than in the more common type 1. SMA type 2 is also known as Dubowitz disease or intermediate SMA. There’s no cure for SMA. But in ...About SMA. Our Research. Drugs in Development. Drugs Discovery Assets. The mission of the Spinal Muscular Atrophy Foundation is to accelerate the development of treatments …Cure SMAOn Tuesday, February 4 th, at 11am CST (9am PST/10am MST/12pm EST) Biogen and Cure SMA will co-host a webinar for the SMA community. During the webinar, you’ll hear from Biogen about the latest information on its SPINRAZA clinical trial, DEVOTE, a Phase 2/3 randomized, controlled dose-escalating study with infantile and later-onset …This work was supported by Cure SMA/Families of SMA Canada (Grant number KOT-1819 and KOT-2021); Muscular Dystrophy Association Inc. (USA) (Grant number 575466); and Canadian Institutes of Health ...Cure SMA is pleased to announce the launch of an expanded Phase 3 of the Real World Evidence Collaboration. The collaboration was established to leverage the experience, expertise and resources of pharmaceutical and biotechnology companies and nonprofit organizations involved in development of SMA therapeutics to guide the future …In June, SMA researchers and clinicians from around the world met in Anaheim, CA, for the 2022 Annual SMA Research and Clinical Care Meeting. There they shared their most recent data with the goal of accelerating the pace of research into SMA treatments and achieving excellence in SMA clinical care.…In June, SMA researchers and clinicians from around the world met in Anaheim, CA, for the 2022 Annual SMA Research and Clinical Care Meeting. There they shared their most recent data with the goal of accelerating the pace of research into SMA treatments and achieving excellence in SMA clinical care.…Cure SMA leads the way to a world without spinal muscular atrophy (SMA), the number one genetic cause of death for infants. We fund and direct comprehensive research that drives breakthroughs in treatment and care, and we provide individuals with SMA and their families the support they need for today. SMA Voice of the Patient Report. Cure SMA and its partners publish papers concerning important research on spinal muscular atrophy (SMA). Below is the latest SMA Industry Collaboration and Cure SMA published research relevant to the treatment and care of SMA. Quick Links Cure SMA Funded Research Publications Be sure you check out below ... Cure SMA is a nonprofit organization that funds research and advocates for people with spinal muscular atrophy (SMA), a genetic neuromuscular disease. Learn about the latest news, events, …September 12, 2019 / No Comments / Uncategorized. The annual SMA Researcher Meeting is the largest research meeting in the world specifically focused on SMA. This year, we had a record setting 735 attendees join together in Anaheim, CA. The goal of the meeting is to create open communication of early, unpublished data, accelerating the pace of ...The status of newborn screening for SMA across the U.S. is shown on the following map — with all 50 states, plus Washington, D.C., screening for SMA. Within 6 years of SMA being added to the federally recommended list of diseases to screen for at birth, Cure SMA and its advocates have ensured that 100% of babies born in the U.S. are now ...The Cure SMA drug pipeline identifies four possible treatment targets: Replacement or correction of the faulty SMN1 gene. Modulation of the low functioning SMN2 “back-up gene.”. Muscle protection to prevent or restore the loss of muscle function in SMA. Neuroprotection of the motor neurons affected by loss of SMN protein.Cure SMA is excited to announce that we will reunite the SMA community in-person for the 2022 Annual SMA Conference in Anaheim, CA–Thursday, June 16 through Sunday, June 19, 2022. If the unexpected circumstances surrounding the pandemic have shown us anything, it is how impactful this one week of the…Cure SMA is pleased to announce the launch of an expanded Phase 3 of the Real World Evidence Collaboration. The collaboration was established to leverage the experience, expertise and resources of pharmaceutical and biotechnology companies and nonprofit organizations involved in development of SMA therapeutics to guide the future …Learn about the FDA-approved treatments for spinal muscular atrophy (SMA), a genetic condition that causes muscle weakness and atrophy. Find out how they work, who …Cure SMA is excited to officially open registration for our Spring 2024 Walk-n-Roll events! By participating in our Walk-n-Roll, you can make a real difference in the lives of those affected by SMA. Here's how you can get started: Register to join OR create a team: Registration is free for everyone….This work was supported by Cure SMA/Families of SMA Canada (Grant number KOT-1819 and KOT-2021); Muscular Dystrophy Association Inc. (USA) (Grant number 575466); and Canadian Institutes of Health ...At the end of June, SMA researchers and clinicians from around the world met in Orlando, Florida, for the 2023 Annual SMA Research & Clinical Care Meeting. The annual meeting provides an opportunity for SMA scientists and clinicians to share their most recent discoveries and learnings, and is an…Make today a breakthrough. A spinal muscular atrophy (SMA) diagnosis must be confirmed through genetic testing. SMA is diagnosed after noticing symptoms of SMA, through newborn screening, or via prenatal testing. Early Symptoms of SMA SMA should be suspected when someone presents with a loss of motor strength and/or not…Cure SMA leads the way to a world without spinal muscular atrophy (SMA), the number one genetic cause of death for infants. We fund and direct comprehensive research that drives breakthroughs in treatment and care, and we provide individuals with SMA and their families the support they need for today. Make today a breakthrough. A team approach and recent medical advances have improved the outlook for infants and children with spinal muscular atrophy (SMA). Cure SMA is here to serve as part of your support team with education, resources, and guidance at every step of your child's SMA journey. Quick…. Cure SMA's national support programs are available to all individuals with spinal muscular atrophy (SMA) and their families who reside in the U.S. Most of these resources are available at no cost. Quick Links Support Services No matter your connection to SMA, we're committed to helping you navigate your journey.…We are pleased to share the following SMA community letter from our partners at Genentech on their clinical development programs and initiatives. Dear SMA Community, Summer is upon us and so are a number of developments we are pleased to share with the SMA community. We are enjoying interacting with…The organization’s grassroots efforts give thousands of families new hope by securing widespread, state-by-state screening for SMA at birth Within three years of spinal muscular atrophy (SMA) being added to the federally recommended list of diseases to screen for at birth, Cure SMA is celebrating a significant milestone—85 percent of …Aquatic therapy is a valuable exercise for those with SMA. “Any exercise is more engaging when it is fun. And you are more likely to return to it, push yourself, and realize the benefits from being in the water,” says Martyn. Water allows for ease of active movement, variations of stability levels, and the ability to support or challenge ...New Zolgensma data demonstrate age-appropriate development when used early, real-world benefit in older children, and durability 5+ years post-treatment. Novartis Gene Therapies recently shared new data that reinforce the transformational benefit of Zolgensma (onasemnogene abeparvovec), a one-time treatment for spinal muscular … SMA Voice of the Patient Report. Cure SMA and its partners publish papers concerning important research on spinal muscular atrophy (SMA). Below is the latest SMA Industry Collaboration and Cure SMA published research relevant to the treatment and care of SMA. Quick Links Cure SMA Funded Research Publications Be sure you check out below ... Cure SMA’s advocacy agenda was developed in response to direct feedback from the SMA community. We collected ideas from active members of the SMA community and then used a survey to establish our top priorities. As a result, we have created the toolkit below to help anyone advocating for these important issues during the 118th Congress. ...SMA Voice of the Patient Report. Cure SMA and its partners publish papers concerning important research on spinal muscular atrophy (SMA). Below is the latest SMA Industry Collaboration and Cure SMA published research relevant to the treatment and care of SMA. Quick Links Cure SMA Funded Research Publications Be sure you check out below ...Each year, Cure SMA invites scientists from around the world to submit funding proposals for basic research projects that address specific unanswered questions in …The 2018 SMA Standards of Care recommendations were published in Neuromuscular Disorders in February 2018 and March 2018 and are available online through Open Access for families and healthcare providers. These documents are updates of the Standard of Care document issued in 2007.The 2018 recommendations …Jun 15, 2023 · Fall 2023 Walk-n-Roll Events. June 8, 2023. Posted in Events & Fundraising, Front Page News. Cure SMA invites you to join us at one of our Fall 2023 Walk-n-Roll Events. We believe that every individual deserves a chance to lead […] Read More ›. The Wait is Over! Register for a Spring Walk-n-Roll. February 6, 2023. The Cure SMA colors are used to represent the entire SMA community and all the hard work and efforts that are put in towards research, care, and support all year long. Check out the calendar for this year's SMA Awareness Month building lightings! Be sure to snag a photo of your local lighting and send it to us at [email protected]. Cure SMA's Walk-n-Roll program are nationwide community fundraising and awareness events. Think of this celebratory environment almost like a block party just for the SMA community. There are games and activities, music, light refreshments, and community celebration for fundraising efforts and the progress we have seen for the spinal muscular ...The Family Friendly Research Poster Session will be held on Saturday, June 29th from 6:30pm to 8:00pm at the 2019 Annual SMA Conference. The Family Friendly Research Poster Session allows for one-on-one interactions between families and researchers. Cure SMA has invited researchers, who are attending SMA …Biogen’s DEVOTE study is designed to evaluate the safety, tolerability, and potential for even greater efficacy of SPINRAZA when administered at a higher dose than currently approved for the treatment of spinal muscular atrophy (SMA). The Phase 2/3 randomized, controlled, dose-escalating study will be conducted at approximately 60 …Cure SMA accepts donations online, over the phone, or via mail. We’ve already invested more than $82 million in research, and your support will allow us to continue funding the discoveries that will lead to more treatments and a cure for SMA. Your gift will also support vital programs for individuals with SMA and their families.SMA Awareness Month strives to raise awareness of the condition caused by the deficiency of a motor neuron protein called SMN and other rare forms of SMA that stem from chromosome mutations. This month, Cure SMA is offering a variety of ways that you can participate by advocating, giving, fundraising, educating, and raising awareness of …SMA Awareness Month 2024 Coming Soon in August 2024 Spinal muscular atrophy (SMA) is a progressive neurodegenerative disease that affects the motor nerve cells in the spinal cord and impacts the muscles used for activities such as breathing, eating, crawling, and walking. Learn About SMA Awareness Month August is…September 12, 2019 / No Comments / Uncategorized. The annual SMA Researcher Meeting is the largest research meeting in the world specifically focused on SMA. This year, we had a record setting 735 attendees join together in Anaheim, CA. The goal of the meeting is to create open communication of early, unpublished data, accelerating the pace of ...Jul 26, 2023 · A previous research study published in 2021 found that a gene therapy similar to an FDA-approved SMA treatment for humans caused unwanted side effects in healthy mice. Through experiments using the FDA-approved treatment in SMA mice, Dr. Balch’s lab showed that the approved drug is unlikely to cause the types of side effects that occurred in ... The presentation will draw from the community viewpoints we have collected from focus groups, surveys, and the Voices of SMA project. Cure SMA also provided funding support for this meeting. The workshop will take place at EMA’s premises in London on November 11, 2016. The entire day will be broadcast live and can be seen on the EMA’s website. SMA Industry Collaboration. The Cure SMA Clinical Trial Readiness Program is an initiative developed under the SMA Industry Collaboration. Our goal is to alleviate challenges related to site capacity and enhance patient access to SMA clinical trials. The program offers resources for clinical research sites that seek to evaluate and optimize ... Cure SMA is excited to announce that we will reunite the SMA community in-person for the 2022 Annual SMA Conference in Anaheim, CA–Thursday, June 16 through Sunday, June 19, 2022. If the unexpected circumstances surrounding the pandemic have shown us anything, it is how impactful this one week of the year is for individuals, … Cure SMA rates among the top charities in the U.S. and is committed to demonstrating the highest degree of accountability and transparency. Make today a breakthrough. $0.80 of every dollar spent funds research, services, and support for individuals with spinal muscular atrophy (SMA) and helps raise awareness of SMA. other questions, call Cure SMA at 800.886.1762, or email [email protected]. WHAT’S INSIDE WHAT YOU SHOULD DO NOW. 4 You may hear people refer to SMA “types.” Before newborn screening for SMA, patients were often diagnosed only after symptoms appeared and were then categorized into four main types depending onAbout Cure SMA. Cure SMA is a voluntary-driven, non-profit organization dedicated solely to eradicating SMA by promoting and supporting research, helping families cope through informational programs and support, and educating the public and the medical community about SMA. Spinal muscular atrophy is a motor neuron disease.Cure SMA is happy to announce the schedule for the 2020 Summit of Strength Program! Currently entering its third year, we have brought together nearly 3,000 community members from across the U.S.! Summits are crafted to provide people of all ages and types of SMA, and their caregivers, the opportunity to network and learn about the latest …Cure SMA’s 38 page report includes more than 150 first-person experiences from adults with SMA and families with children with SMA from across the country. The report also includes recommendations for improving air travel for passengers with disabilities, particularly those who use wheelchairs.The Discovery of Spinraza. SMA is caused by a mutation in the survival motor neuron gene 1 (SMN1). In a healthy person, this gene produces a protein—called survival motor neuron protein or SMN protein—that is critical to the function of the nerves that control our muscles. Without it, those nerve cells cannot properly function and ...We are pleased to share the following SMA community letter from our partners at Genentech on their clinical development programs and initiatives. Dear SMA Community, Summer is upon us and so are a number of developments we are pleased to share with the SMA community. We are enjoying interacting with…September 12, 2019 / No Comments / Uncategorized. The annual SMA Researcher Meeting is the largest research meeting in the world specifically focused on SMA. This year, we had a record setting 735 attendees join together in Anaheim, CA. The goal of the meeting is to create open communication of early, unpublished data, accelerating the pace of ...However, it is now apparent that none of these therapies will cure SMA alone. In this review, we discuss the three currently licensed therapies for SMA, briefly …Feb 26, 2020 · Evrysdi. Evrysdi is the first oral medication approved for the treatment of SMA. It’s composed of a small molecule that works by modifying the amount of SMN protein that’s made from the SMN2 ... Make today a breakthrough. A spinal muscular atrophy (SMA) diagnosis must be confirmed through genetic testing. SMA is diagnosed after noticing symptoms of SMA, through newborn screening, or via prenatal testing. Early Symptoms of SMA SMA should be suspected when someone presents with a loss of motor strength and/or not…You can learn more about these SMA therapies by visiting these links: If you have any questions about the information here, contact our national office at (800) 886-1762 or email [email protected], and a member of our team will be in touch. For Healthcare providers: We invite you to update or add your treatment location to our location finder ...Make today a breakthrough. Did you know you may be able to double your support for Cure SMA and our spinal muscular atrophy (SMA) community without giving a dollar more? If you or your partner works for a company that offers a matching gift program, you canThe Cure SMA Walk-n-Roll is a fun, family-friendly event that supports Cure SMA’s mission of driving breakthroughs in treatment and care and providing families the support they need for today. We welcome you to join us as an individual or start a team with your family, friends, co-workers, and neighbors.The…Cure SMA is excited to officially open registration for our Spring 2024 Walk-n-Roll events! By participating in our Walk-n-Roll, you can make a real difference in the lives of those affected by SMA. Here's how you can get started: Register to join OR create a team: Registration is free for everyone….Cure SMA and Genentech to Co-Host SMA Community Webinar Cure SMA and Genentech will hold a joint webinar on the approval of Evrysdi on Tuesday, August 18, 2020 at 12 p.m. (CT). We will be sharing the latest on this news and will include a Q&A session based on questions submitted in advance of the webinar.About Cure SMA. Cure SMA is a voluntary-driven, non-profit organization dedicated solely to eradicating SMA by promoting and supporting research, helping families cope through informational programs and support, and educating the public and the medical community about SMA. Spinal muscular atrophy is a motor neuron disease. For the past six years, the Cure SMA Community Update Survey has collected data and information on our SMA community’s experiences and daily challenges. Our top priority is to represent the voice from the whole community so we can drive research and care to meet needs of everyone impacted by SMA. Completing this survey is one tangible, and ... Spinal muscular atrophy (SMA) refers to a group of hereditary diseases that can damage and kill specialized nerve cells in the brain and spinal cord (motor neurons). Motor neurons control movement in the arms, legs, face, chest, throat, and tongue, as well as skeletal muscle activity, such as speaking, walking, swallowing, and breathing.SMA Voice of the Patient Report. Cure SMA and its partners publish papers concerning important research on spinal muscular atrophy (SMA). Below is the latest SMA Industry Collaboration and Cure SMA published research relevant to the treatment and care of SMA. Quick Links Cure SMA Funded Research Publications Be sure you check out below ...Jun 29, 2022 · There is new hope (and a new treatment) for young children diagnosed with SMA. Many now have a fighting chance — a life-saving, dramatically improved prognosis and quality of life — thanks to a new, effective treatment and promising developments on the horizon. But early diagnosis and early treatment are key. SMA (spinal muscular atrophy) is a genetic disease that robs people of physical strength by affecting the motor nerve cells in the spinal cord, taking away the ability to walk, eat, or breathe. It is the number one genetic cause of death for infants. SMA is caused by a mutation in the survival motor neuron gene 1 (SMN1). September 12, 2019 / No Comments / Uncategorized. The annual SMA Researcher Meeting is the largest research meeting in the world specifically focused on SMA. This year, we had a record setting 735 attendees join together in Anaheim, CA. The goal of the meeting is to create open communication of early, unpublished data, accelerating the pace of ...In a previous Community Spotlight, we talked about how Ben has teamed up with his good friend, Dana Perrella, to raise money for Cookies4SMA. Her fundraising organization, Cookies4Cures, is partnering with Cure SMA to raise $50,000 for SMA research in 2020. You can help in this cause by donating online via her GoFundMe page, …Cure SMA is pleased to announce the launch of the second annual State of SMA report. The purpose of this report is to share highlights from Cure SMA’s three databases: a patient-reported database with data from over 9,700 affected individuals worldwide that also incorporates longitudinal data from our annual community…With an incidence of approximately one in 11,000, more than 360 infants will be born annually with spinal muscular atrophy (SMA). Newborn screening can help to pre-empt irreversible motor neuron loss, increase prompt intervention, and eliminate long diagnostic delays. The impact of early diagnosis has been demonstrated through several … This booklet offers a foundation for understanding SMA if you are a parent or a patient learning about SMA for the first time. Make today a breakthrough. With publications like our Care Series Booklets, along with other helpful resource booklets, Cure SMA is committed to providing our spinal muscular atrophy (SMA) community with the information ... Learn about the causes, types, symptoms, diagnosis, and treatment of SMA, a group of hereditary diseases that damage motor neurons. Find out about the …Each year, Cure SMA invites scientists from around the world to submit funding proposals for basic research projects that address specific unanswered questions in …Jun 29, 2022 · There is new hope (and a new treatment) for young children diagnosed with SMA. Many now have a fighting chance — a life-saving, dramatically improved prognosis and quality of life — thanks to a new, effective treatment and promising developments on the horizon. But early diagnosis and early treatment are key. SMA and Genetics. Spinal muscular atrophy (SMA) is caused by a mutation in the survival motor neuron gene 1 (SMN1). In a healthy person, this gene produces a protein—called survival motor neuron protein or SMN protein—that is critical to the function of the nerves that control our muscles. Without it, those nerve cells cannot properly ...
Scholar Rock, a clinical-stage biopharmaceutical company focused on the treatment of serious diseases in which protein growth factors play a fundamental role, today announced that the U.S. Food and Drug Administration (FDA) has granted Rare Pediatric Disease (RPD) designation for SRK-015 for the treatment of Spinal Muscular Atrophy …. Ne lakeview
Cure SMA and its partners in industry, healthcare, and research created the Clinical Trial Readiness Program to increase the number of well-prepared, patient-centered SMA clinical trial sites. Increasing the number of clinical trial sites will make SMA research participation an option for more SMA-affected individuals, accelerating the progress ...May 15, 2017 · Cure SMA is dedicated to the treatment and cure of spinal muscular atrophy (SMA)—a disease affecting motor neurons, that robs patients of their ability to walk, eat and even breathe. Since 1984 ... Learn more. We believe that substantial and strategic investment in research is how we'll achieve our mission. We will not stop until we have a cure for spinal muscular atrophy (SMA)! For researchers working in SMA, Cure SMA's investment in research and the researcher community includes the following: Funding Opportunities We've invested….About. Spinal Muscular Atrophy (SMA) is a motor neuron disease. The motor neurons affect the voluntary muscles that are used for activities such as crawling, walking, head and neck control, and swallowing. It is a relatively common “rare disorder”: approximately 1 in 6000 babies born are affected, and about 1 in 40 people are genetic carriers.However, it is now apparent that none of these therapies will cure SMA alone. In this review, we discuss the three currently licensed therapies for SMA, briefly …Cure SMA and Genentech to Co-Host SMA Community Webinar Cure SMA and Genentech will hold a joint webinar on the approval of Evrysdi on Tuesday, August 18, 2020 at 12 p.m. (CT). We will be sharing the latest on this news and will include a Q&A session based on questions submitted in advance of the webinar.Introduction. Spinal muscular atrophy (SMA), a childhood-onset motor neuron disease, has historically been the most frequent genetic cause of infant mortality, 1 although this is likely to change with the recent therapeutic “revolution.” SMA, caused by mutations in the Survival Motor Neuron 1 (SMN1) gene, leads to loss of SMN protein expression.Often, the musculoskeletal team for an individual with SMA will include: Occupational Therapists (OT) work primarily with the arms and hands, focusing on activities like feeding, dressing, and other skills. They may recommend or make splints and teach exercises to maintain range of motion and improve function.At the end of June, SMA researchers and clinicians from around the world met in Orlando, Florida, for the 2023 Annual SMA Research & Clinical Care Meeting. The annual meeting provides an opportunity for SMA scientists and clinicians to share their most recent discoveries and learnings, and is an…CURE SMA 2 • Improved Growth: Gaining weight while growing in height is essential for good health. Having enough energy (calories) helps keep the body growing by supporting lung tissue and the heart muscle. • Better Breathing: Growth in length helps with ... The Summit of Strength Program is a free half-day educational and networking event hosted by Cure SMA, made available for people of all ages and types of SMA and their caregivers. Register today for your local summit and get ready to connect with your community and learn about the latest advances in treatment, care, advocacy, and support. Introduction Understanding clinical trial experiences can illuminate opportunities to optimize trial design and management, with potential benefits for recruitment and retention. This study sought to better understand clinical trial participant experiences and attitudes within spinal muscular atrophy (SMA), and how the evolving treatment …Fall 2023 Walk-n-Roll Events. June 8, 2023. Posted in Events & Fundraising, Front Page News. Cure SMA invites you to join us at one of our Fall 2023 Walk-n-Roll Events. We believe that every individual deserves a chance to lead […] Read More ›. The Wait is Over! Register for a Spring Walk-n-Roll. February 6, 2023. Cure SMA leads the way to a world without spinal muscular atrophy (SMA), the number one genetic cause of death for infants. We fund and direct comprehensive research that drives breakthroughs in treatment and care, and we provide individuals with SMA and their families the support they need for today. Required fields are marked. During our past fiscal year—from July 1, 2019 to June 30, 2020—Cure SMA funded more than $9 million in new and ongoing research and care initiatives. This money will be used strategically to help accelerate research and ensure we are developing treatments and protocols for all types, ages, and stages…..